index - Repeat Expansions & Myotonic Dystrophy (REDs)

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Expression Gene therapy CRISPR/Cas9 Cell culture model Aging Centronuclear myopathy Animals Myotonic dystrophy Glucocorticoids Neuron Thérapie génique Brain dysfunction Acute coronary syndrome DMPK Myotonic dystrophy type 1 CRISPRi Therapy Acetylcholinesterase deficiency Antisense oligonucleotides PacBio RNA biology Transgenic mouse Mouse model Cytoskeleton Humans Gene Therapy Male Diaphragm PCR Astrocyte Dystrophie myotonique Cell penetrating peptide Glucocorticoid-receptor MBNL Acetylcholinesterase knockout mouse Trinucleotide repeat expansion Intermediate filament Myotonic Dystrophy type 1 Transgenic mouse model RNA splicing Fibrosis Exercise Skeletal muscle Cardiac muscle Hypoxia Heart failure Maximal force Dynamin 2 Oligodendrocytes In vivo Oligodendrocyte Glutamate DMSXL mice Heart Brain Myostatin Exercice Dystrophin Central nervous system Dilated cardiomyopathy Endurance training DM1 Genotype phenotype correlation Alternative splicing CMS Trinucleotide Repeat Expansion Myotonic Dystrophy Type 1 CTG repeat contractions Antisense oligonucleotide Desmin Motoneuron Astrocytes Mouse models RNA interference Duchenne muscular dystrophy Quantitative microdialysis Knockout GSK3␤ GABA Long read sequencing Myotonic dystrophy mouse models CTG repeats KNOCKOUT MICE CONGENITAL MYATHENIC SYNDROME Myotonic Dystrophy Dystrophie Myotonique Transcriptomics AAV Muscle Autophagy Myelin ARN BIOLOGIE MOLECULAIRE Gene editing ACETYLCHOLINESTERASE Muscular dystrophy Mice Cell model Glial cells CTG repeat instability