index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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DMO Diseases Gene Expression Regulation/drug effects Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Duchenne DMD dystrophy Duchenne muscular dystrophy DMD Skeletal muscle Centronuclear myopathy Cells Multi exon skipping Human Umbilical Vein Endothelial Cells Cardiomyopathie Cell Line NAD+ LncRNA Activin Receptors Metabolism Becker muscular dystrophy Delivery BMD Inhibitors Cell homeostasis LncARN Ex-vivo Liver Myogenesis Energy Metabolism/drug effects Inbred C57BL Invivo Dystrophin-EGFP MiARN Homeostasis Dystrophine DHPR α1S Genomic Muscle development Molecular docking Muscular Atrophy Hear Muscle Strength Dynamin 2 CaVβs Immunoglobulin Fc Fragments/pharmacology Cardiomyopathy L-Type Long noncoding RNA Mitochondrial fission Multi resolution modeling Cachexia Autophagy Epigenetics Humans Animals Calcium Becker muscular dystrophy BMD Dystrophin Drp1 Morphogenesis Mdx mouse NNOS Gene expression Allele‐specific silencing therapy Modificateurs de gènes Calcium Channels CaV subunits Inbred mdx Muscle Biology MES Gene modifiers LKB1 DMD Animal/physiopathology Knockout Génomique Dystrophie Musculaire de Duchenne DMD Muscular Dystrophy Male Hepatocellular carcinoma Mice Dystrophie Musculaire de Becker BMD Muscles/physiopathology Exon skipping Muscle Multiresolution modeling Base Sequence Duchenne muscular dystrophy Molecular Sequence Data Cultured Myotendinous junction Cell Biology Antisense oligonucleotides CTNNB1 Dystrophie musculaire de Becker Muscular dystrophy CD38 Dystrophy Becker BMD muscular dystrophy Clinical trials Long QT Dystrophin central domain