Loading...
Dernières publications
-
Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
-
A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
-
Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
47
Publications avec texte intégral
Open Access
73 %
Mots clés
DMO
Diseases
Gene Expression Regulation/drug effects
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Duchenne DMD dystrophy
Duchenne muscular dystrophy DMD
Skeletal muscle
Centronuclear myopathy
Cells
Multi exon skipping
Human Umbilical Vein Endothelial Cells
Cardiomyopathie
Cell Line
NAD+
LncRNA
Activin Receptors
Metabolism
Becker muscular dystrophy
Delivery
BMD
Inhibitors
Cell homeostasis
LncARN
Ex-vivo
Liver
Myogenesis
Energy Metabolism/drug effects
Inbred C57BL
Invivo
Dystrophin-EGFP
MiARN
Homeostasis
Dystrophine
DHPR α1S
Genomic
Muscle development
Molecular docking
Muscular Atrophy
Hear
Muscle Strength
Dynamin 2
CaVβs
Immunoglobulin Fc Fragments/pharmacology
Cardiomyopathy
L-Type
Long noncoding RNA
Mitochondrial fission
Multi resolution modeling
Cachexia
Autophagy
Epigenetics
Humans
Animals
Calcium
Becker muscular dystrophy BMD
Dystrophin
Drp1
Morphogenesis
Mdx mouse
NNOS
Gene expression
Allele‐specific silencing therapy
Modificateurs de gènes
Calcium Channels
CaV subunits
Inbred mdx
Muscle Biology
MES
Gene modifiers
LKB1
DMD
Animal/physiopathology
Knockout
Génomique
Dystrophie Musculaire de Duchenne DMD
Muscular Dystrophy
Male
Hepatocellular carcinoma
Mice
Dystrophie Musculaire de Becker BMD
Muscles/physiopathology
Exon skipping
Muscle
Multiresolution modeling
Base Sequence
Duchenne muscular dystrophy
Molecular Sequence Data
Cultured
Myotendinous junction
Cell Biology
Antisense oligonucleotides
CTNNB1
Dystrophie musculaire de Becker
Muscular dystrophy
CD38
Dystrophy
Becker BMD muscular dystrophy
Clinical trials
Long QT
Dystrophin central domain